- US FDA approves PTC Therapeutics’ metabolic disorder drug Reuters
- PTC’s PKU drug scores US approval FirstWord Pharma
- FDA Approves Sepiapterin for Adults, Children Living With Phenylketonuria Pharmacy Times
- PTC Therapeutics Gains FDA Approval for Sephience TipRanks
- WATCH: Experts react to the FDA approval of sepiapterin to treat PKU Contemporary Pediatrics