US FDA approves PTC Therapeutics' metabolic disorder drug – Reuters

  1. US FDA approves PTC Therapeutics’ metabolic disorder drug  Reuters
  2. PTC’s PKU drug scores US approval  FirstWord Pharma
  3. FDA Approves Sepiapterin for Adults, Children Living With Phenylketonuria  Pharmacy Times
  4. PTC Therapeutics Gains FDA Approval for Sephience  TipRanks
  5. WATCH: Experts react to the FDA approval of sepiapterin to treat PKU  Contemporary Pediatrics

Continue Reading