Mifepristone, a glucocorticoid blocker, increased survival and muscle size in a mouse model of spinal muscular atrophy (SMA), according to a recent study.
Combining mifepristone with a gene therapy construct similar to the one used in Zolgensma…

Mifepristone, a glucocorticoid blocker, increased survival and muscle size in a mouse model of spinal muscular atrophy (SMA), according to a recent study.
Combining mifepristone with a gene therapy construct similar to the one used in Zolgensma…